REGENXBIO Inc. (Nasdaq: RGNX), a clinical-stage biotechnology company, based in Rockville, Maryland, has reported positive interim data from an ongoing Phase II “ALTITUDE” trial of… Read More »Regenxbio Inc.’s gene therapy treatment (RGX-314) for diabetic retinopathy (DR) reports positive interim data from Phase II.
Teva Pharmaceitical (NYSE and TASE: TEVA) has announced that the UK Medicines & Healthcare Regulatory Agency (MHRA) is to grant a licence for “Ongavia”, a… Read More »Teva Pharmaceutical Industries Ltd., (NYSE and TASE: TEVA), has announced the licencing, the UK MHRA, of a biosimilar (“Ongavia”) to Lucentis (ranibizumab).
MeiraGTx (Nasdaq: MGTX) has announced that additional clinical data from the Phase 1/2 trial of botaretigene sparoparvovec for the treatment of X-linked Retinitis Pigmentosa (XLRP)… Read More »MeiraGTx (NASDAQ: MGTX), a UK gene therapy company, has announced preliminary efficacy data from a gene therapy for XLRP patients
Opus Genetics Inc., a private ocular gene therapy company based in Raleigh, North Carolina, has announced a strategic manufacturing services agreement with National Resilience, Inc.… Read More »Opus Genetics Inc., has announced a strategic manufacturing services agreement with National Resilience, Inc., for the development of LCA treatments
Ocugen Inc., (NASDAQ:OCGN), an ophthalmic biopharmaceutical company based in Malvern, Pennsylvania, has announced that the first patient has been dosed in a Phase 1/2 clinical… Read More »Ocugen Inc., (NASDAQ: OCGN) has announced the launch of a Phase 1/2 study for a modifier gene therapy candidate treating retinitis pigmentosa (RP)
Aldeyra Therapeutics, Inc. (NASDAQ: ALDX), a clinical stage company based in Lexington, Massachusetts, has reported the initiation of a Phase 2 clinical trial of ADX-2191… Read More »Aldeyra Therapeutics Inc., (NASDAQ: ALDX) reports the launch of a Phase 2 study for methotrexate to treat Pro23His retinitis pigmentosa (RP)
A Dutch biotechnology company, ProQR Therapeutcis N.V., (NASDAQ:PRQR), Leiden, has announced the results of a Phase 2/3 study for the treatment of Leber Congenital Amaurosis… Read More »ProQR Therapeutics N.V. (NASDAQ: PRQR), announces top-line results for the treatment of a novel RNA therapy (“Sepofarsen [QR-110]”) for LCA10
A French bioelectronics company “Pixium Vision SA”, based in Paris, has announced the implantation of an artificial retina in a first patient in the UK. … Read More »Pixium SA has announced the first UK patient enrolled in a “PRIMAvera” study with the implantation of a bionic artificial retina
Neurogene Inc. based in Manhattan, New York City, has announced that the U.S. Food and Drug Administration (FDA) has cleared the company’s Investigational New Drug… Read More »Neurogene Inc. (NYC, USA) has announced to become the first investigative treatment of both neurodegenerative and ocular disease manifestations of Batten Disease.
In follow up the recent French Competent Authority granting of a Cohort Temporary Authorization for Use (“ATU de Cohorte” or ATUc) in July in 2021,… Read More »GenSight Biologics has reported recent research on how gene therapy transfer works migrating vectors from treated to control eyes.