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Treatment of a common X-linked form of retinitis pigmentosa by gene augmentation is demonstrated in canine models

New research focused on the treatment of a common form of retinitis pigmentosa (RP), X-linked retinitis pigmentosa, has demonstrated the efficacy of gene augmentation to prevent disease development and restore photoreceptor morphology. The research extends the potential application of gene therapy technologies beyond the initial studies on recessive disorders such as Leber’s congenital amaurosis (LCA) and suggests that some of the more common forms of RP may also benefit from strategies aimed at treating the very root cause of many such retinal degenerative pathologies.